More research is needed to confirm gray matter, the darker tissue found in the brain and spinal cord, “as a potential disease ...

A woman with SMA type 3 became pregnant while on Spinraza treatment and gave birth to a healthy child, per a case report.

Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...

Novartis has reported positive topline outcomes from the Phase III STEER trial of an ... in treating individuals with spinal muscular atrophy (SMA) Type 2. The randomised, sham-controlled study ...

Centre abdicates its constitutional obligation, criticises patients and experts on SMA issue: Our Bureau, New Delhi Friday, January 24, 2025, 18:15 Hrs [IST] Patients and public h ...

The health activists argue that the government is empowered with effective law and policy tools and therefore should ...

Health activists demand government action to reduce the cost of SMA medicines, citing constitutional obligations and ...

Opens in a new tab or window Researchers evaluated oxygen saturation and arterial CO2 variables to screen for sleep disordered breathing in children with SMA type 1-3. Of the measures evaluated ...

Intrathecal onasemnogene abeparvovec improved HFMSE scores in patients with SMA type 2, indicating enhanced motor function. The STEER study confirmed the therapy's favorable safety profile ...