More research is needed to confirm gray matter, the darker tissue found in the brain and spinal cord, “as a potential disease ...
One such condition is Spinal Muscular Atrophy (SMA), a genetic disorder affecting infants and young children, impacting their movement and muscle function. SMA is a genetic disorder of movement ...
Novartis has reported positive phase 3 results with intrathecal dosing of its spinal muscular atrophy (SMA) gene therapy Zolgensma, which could extend the range of children eligible for the drug.
The device is designed to aid children diagnosed with cerebral palsy, spinal muscular atrophy, hemi and paraplegia ... video released by the company features Alex, a young adult, who testifies ...
The mutation that causes Spinal Muscular Atrophy (SMA) can be detected in a prenatal screen. But a parent's decision to test for this terrible disease is not as easy as you would think.
Considering taking supplements to treat spinal muscular atrophy? Below is a list of common natural remedies used to treat or reduce the symptoms of spinal muscular atrophy. Follow the links to ...
Health activists and patients with spinal muscular atrophy (SMA) have refuted the Central government’s affidavit in the Kerala High Court and demanded urgent action to reduce the cost of ...
Back to Healio Topline results from a phase 3 clinical trial showed an investigational gene therapy for young people with spinal muscular atrophy type 2 increased mobility and slowed disease ...
The Amsterdam-based biotech firm said that its melt curve analysis-based test is used as a first-tier genetic screening tool to aid the diagnosis of SMA.
The US Food and Drug Administration (FDA) has accepted Biogen’s supplemental New Drug Application (sNDA) and the European ...
For children with SMA, assistive devices -- walkers, wheelchairs, standers, and more -- are the key to staying active. Learn which ones may help your child.