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Spinraza remains a big product for Biogen, but has seen its sales go into reverse as competition in SMA treatment has emerged ...

Sidra Medicine, a member of Qatar Foundation, has established a gene therapy centre to treat rare genetic diseases such as ...

Asher Cantrell, diagnosed with SMARD 1, has received experimental gene therapy after social media support and is currently ...

In a LinkedIn post, Monisha shared the challenges of travelling with her 14-year-old daughter, Keya, who has Spinal Muscular ...

The announcement was made at Arab Health 2025 where Sidra Medicine will highlight its international patient service programmes ...

Application is supported by results from the DEVOTE study, which suggested that two doses of Spinraza (nusinerse) 50 mg taken ...

Press releaseGenethon and Eukarÿs announce a strategic partnership to develop a breakthrough technology to reduce the biomanufacturing cost of ...

The Amsterdam-based biotech firm said that its melt curve analysis-based test is used as a first-tier genetic screening tool to aid the diagnosis of SMA.

Health activists demand government action to reduce the cost of SMA medicines, citing constitutional obligations and ...

The health activists argue that the government is empowered with effective law and policy tools and therefore should ...