The bill considered today was aimed at forcing more transparency in the attorney general's office and failed on a 67 to 65 vote with no Democrats in support and all Republicans voting in favor.

Grammy-nominated Hozier is known for the hit song Take Me To Church released in 2013. His 2014 a self-titled album made it to ...

Passage Bio is outsourcing future analytical testing services in a cost-cutting move that will further cut its workforce, a ...

Orchard Therapeutics has tasked Robin Kenselaar with accelerating growth of Lenmeldy, the world’s most expensive drug, ...

The Metachromatic Leukodystrophy Initiative (MLDi) critically responds to the findings of Zhang et al. on lentivirus-modified ...

The first baby to have a cord blood sample taken as part of the study at Jessop Wing was Sophia Bird, who was born on December 16, 2024. In a joint statement, Sophia’s mum Alice and dad Robert said: ...

brittle bone disease as well as lesser-known disorders such as metachromatic leukodystrophy (MLD) in hundreds of babies shortly after birth rather than when symptoms might appear later in childhood.

untreated sibling pairs with early-onset metachromatic leukodystrophy* Date/Time: Friday, February 7 at 2:00 p.m. Presenter: Karen Bean Details of the poster presentations are as follows (all ...

untreated sibling pairs with early-onset metachromatic leukodystrophy* Date/Time: Friday, February 7 at 2:00 p.m. Presenter: Karen Bean Details of the poster presentations are as follows (all times in ...

This video was funded by Orchard Therapeutics. This video features insights from leading experts on metachromatic leukodystrophy (MLD), a rare and progressive neurodegenerative lysosomal storage ...

And yet everything is different. July 2024 is when Jasman passed away from a rare condition known as Metachromatic leukodystrophy, often abbreviated as MLD. “MLD causes the brain to separate ...

The family is hoping for a miracle to help with his treatment. The story was shared through the Facebook page "Little Dayton fights with MLD Metachromatic Leukodystrophy", where one post revealed that ...