Metachromatic leukodystrophy is a genetic condition that occurs due to an enzyme deficiency. Patients with this disorder have ...

The bill considered today was aimed at forcing more transparency in the attorney general's office and failed on a 67 to 65 ...

A man is singing for 24 hours straight in Liverpool city centre for a special reason. Jason Allan, 27, from Liverpool city ...

The Metachromatic Leukodystrophy Initiative (MLDi) critically responds to the findings of Zhang et al. on lentivirus-modified ...

This drug treats a debilitating and lethal disease that mostly affects infants called metachromatic leukodystrophy (MLD).

Orchard Therapeutics has revealed its US pricing plans for Lenmeldy, its gene therapy for metachromatic leukodystrophy (MLD), placing a $4.25 million price tag on the one-shot treatment.

Orchard Therapeutics has tasked Robin Kenselaar with accelerating growth of Lenmeldy, the world’s most expensive drug, ...

Orchard Therapeutics' gene therapy for rare childhood disease metachromatic leukodystrophy (MLD) Libmeldy has been rejected for NHS use by NICE in draft guidance. The agency said that while there ...

And yet everything is different. July 2024 is when Jasman passed away from a rare condition known as Metachromatic leukodystrophy, often abbreviated as MLD. “MLD causes the brain to separate ...