Researchers at the University of Pittsburgh say a new minimally invasive intervention can target the root cause of neural function loss.

The evolution of functional assessments for spinal muscular atrophy (SMA) highlights the challenges of adapting pediatric ...

Spinal muscular atrophy (SMA) is a debilitating genetic condition that’s usually fatal by a few years of age. But an ...

Ionis relies on upfront payments and licensing fees from partners, as well as Spinraza royalties, to drive revenue today, but its rapidly advancing portfolio should help diversify revenue. 2025 is ...

The first prenatal therapy for spinal muscular atrophy (SMA) showed promising results, a case report indicated. More than 2 ...

The Muscular Dystrophy Association (MDA) today launched the nation’s largest St. Patrick’s Day fundraising campaign, MDA Shamrocks, as part of its celebration of 75 years of progress and impact in ...

Over the past nine years, patients with spinal muscular atrophy have seen the number of FDA-approved treatment options for ...

SOUTH SAN FRANCISCO, Calif.--(BUSINESS WIRE)--Genentech, a member of the Roche Group (SIX: RO, ROG; OTCQX: RHHBY), announced today that the U.S. Food and Drug Administration (FDA) has approved a New ...

The Texas Coalition for Patients has a legislative priority list that includes restrictions on artificial intelligence and ...

A new electrical stimulation therapy for spinal muscle atrophy (SMA) has shown promise in reactivating motor neurons and ...

Indian Union Muslim League (IUML) member in Rajya Sabha Haris Beeran Friday sought urgent intervention of the Union Health Ministry to allow production of generic medicines for Spinal Muscular Atrophy ...