In a groundbreaking medical achievement, doctors have successfully treated a life-threatening motor neuron disease in a baby ...

The mother took the drug daily for six weeks while the baby herself was given the drug orally, roughly one week after the ...

An infant with a fatal genetic disease has survived past the age of 2 with no signs of the condition, thanks to treatment ...

A mother was given SMA treatment Evrysdi during pregnancy, and her child with SMA, now 2.5, has not shown any signs of the ...