News Medical on MSN2d
Promising results from first prenatal therapy for spinal muscular atrophy
Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before birth. Scientists at St. Jude ...
The American Journal of Managed Care1d
Redefining Functional Measures in SMA: Insights From Clinical Research
The evolution of functional assessments for spinal muscular atrophy (SMA ... AJMC: What is your role as a physical therapist and clinical researcher in the management of patients living with ...
Macleans.ca2d
How Patients Living With Spinal Muscular Atrophy Can Achieve More Through Active Living
Exercise can make a significant difference for patients with SMA by working alongside other medical advancements to improve ...
health.wusf.usf.edu4d
Price of love: Gene therapy gives hope to a child with spinal muscular atrophy
On this episode, an infant with a harrowing diagnosis defies all odds after receiving a $2 million genetic treatment. Then, a ...
Neurology Advisor1d
FDA Approves Tablet Form of Evrysdi for Spinal Muscular Atrophy
The US Food and Drug Administration has approved a new drug application for a tablet version of Evrysdi (risdiplam) for people living with spinal muscular atrophy (SMA).
BioSpace8d
Roche’s Evrysdi Becomes First Pill Cleared for Spinal Muscular Atrophy
The FDA on Wednesday approved the industry’s first-ever tablet treatment for spinal muscular atrophy— Roche ’s SMN2 splicing ...
The American Journal of Managed Care10d
Risdiplam Tablet for Spinal Muscular Atrophy Receives FDA Approval
The 5 mg risdiplam tablet provides the same efficacy and safety for spinal muscular atrophy as the currently available oral ...
Newsday17d
A spine-zapping implant helped 3 people with a muscle-wasting disease walk better
Spinal muscle atrophy or SMA is a genetic disease that ... There is no cure. A gene therapy can save the lives of very young children with a severe form of the disease, and there are some ...
News Medical on MSN17d
Spinal cord stimulation restores neural function, targets key feature of progressive neurodegenerative disease
Boosting communication between the spinal nerves and the muscles using the spinal cord stimulation reverses spinal muscle ...
Science Daily3d
Promising results from first prenatal therapy for spinal muscular atrophy
Scientists report results from a promising new approach to treat the rare neurodegenerative disorder. Spinal muscular atrophy (SMA) is a progressive neurodegenerative disorder set in motion before ...
Healio8d
FDA approves Evrysdi tablets for spinal muscular atrophy
The FDA has approved Evrysdi in tablet form for patients with spinal muscular atrophy aged 2 years and older who weigh more ...