A man is singing for 24 hours straight in Liverpool city centre for a special reason. Jason Allan, 27, from Liverpool city ...

The bill considered today was aimed at forcing more transparency in the attorney general's office and failed on a 67 to 65 ...

Grammy-nominated Hozier is known for the hit song Take Me To Church released in 2013. His 2014 a self-titled album made it to ...

Passage Bio is outsourcing future analytical testing services in a cost-cutting move that will further cut its workforce, a ...

The National Organization for Rare Disorders is a coalition of patient advocacy groups and the first national nonprofit that ...

Orchard Therapeutics has revealed its US pricing plans for Lenmeldy, its gene therapy for metachromatic leukodystrophy (MLD), placing a $4.25 million price tag on the one-shot treatment.

Libmeldy (atidarsagene autotemcel) was approved by the European Commission to treat metachromatic leukodystrophy (MLD) in December 2020, and subsequently rejected for NHS use by NICE last July on ...

In January 2024, the company acquired Orchard Therapeutics Plc, which developed the world's most expensive drug for the treatment of a rare disease called metachromatic leukodystrophy, which is sold ...

A Southern California family is desperate to save the life of their 3-year-old daughter who has been diagnosed with an extremely rare disease. In July 2023, Harlow Prado was diagnosed with a rare ...