The evolution of functional assessments for spinal muscular atrophy (SMA) highlights the challenges of adapting pediatric ...
Exercise can make a significant difference for patients with SMA by working alongside other medical advancements to improve ...
The first prenatal therapy for spinal muscular atrophy (SMA) showed promising results ... which is approved to treat SMA in pediatric and adult patients, and continues to receive the oral drug ...
The Muscular Dystrophy Association (MDA) today launched the nation’s largest St. Patrick’s Day fundraising campaign, MDA Shamrocks, as part of its celebration of 75 years of progress and impact in ...
The tablet formulation can either be swallowed whole or dispersed in a teaspoon of filtered (non-chlorinated) water.
Ionis relies on upfront payments and licensing fees from partners, as well as Spinraza royalties, to drive revenue today, but its rapidly advancing portfolio should help diversify revenue. 2025 is ...
🛀 Ancient luxury: A lavish spa complex with several types of baths and a banquet hall has been unearthed in the ancient ...
PTC Therapeutics (NASDAQ:PTCT – Get Free Report) had its price objective hoisted by Royal Bank of Canada from $60.00 to $63.00 in a research report issued to clients and investors on Tuesday,Benzinga ...